Dr Julien Baruteau is a MRC Clinician Scientist Fellow and Group Leader at University College London Great Ormond Street Institute of Child Health and Consultant in Metabolic Medicine at Great Ormond Street Hospital for Children in London. His research focuses on studying the pathophysiology and developing novel therapies for inherited metabolic diseases. He has developed gene therapy using both viral and non-viral vectors and is the UK chief investigator in first-in-human gene therapy clinical trial. He has expertise in translating academic and industry-led programmes of gene therapies. He is the member of experts’ committees from the European Society of Gene and Cell Therapy, the American Society of Gene and Cell Therapy and the European Society of Human Genetics.